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Show: March 18, 2012:
- Statin Drug Warning From the FDA
- Tanning Bed Addicts
- Black Tea for High Blood Pressure
- Breakthrough Gene Therapy Treats Hemophilia B
- How "Trusting Your Gut" May Help You Win the Office Pool
- Why We Love Fatty Foods
- Doc Chat: Teaching Patients to Eat Healthy
- View all topics for the week
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Breakthrough Gene Therapy Treats Hemophilia B
Host: David Crabb, MD
Interview: Katherine A. High, MD,
professor of pediatrics, University of Pennsylvania School of Medicine
director, Center for Cellular and Molecular Therapeutics, Children's Hospital of Philadelphia
Investigator, Howard Hughes Medical Institute
Hemophilia is a genetic disorder in which the patient’s blood lacks the all-important clotting factor.
Physician and hemophilia researcher Katherine A. High, MD, chats with Sound Medicine’s Dr. David Crabb about the encouraging results of a recent study that injected patients with the correct form of the defective gene.
It may be the first instance of gene therapy successfully used to treat a well-known disease.
Dr. High is a professor of pediatrics at the University of Pennsylvania School of Medicine and director of the Center for Cellular and Molecular Therapeutics at Children's Hospital of Philadelphia. In addition, she is an investigator with Howard Hughes Medical Institute.
Additional Resources:
- For more, see the NYT article, Treatment for Blood Disease Is Gene Therapy Landmark.
- Learn more about Dr. Katherine High and her work.
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